Every year in the UK around 70 children are diagnosed with rhabdomyosarcoma, a cancer that resembles developing skeletal muscle. The available treatments have remained largely unchanged for 20 years and, although they do work for some children, can cause long-term side effects that seriously affect their normal development. New treatments are needed so that more children can recover and lead a normal life.
Over the last 20 years or so there has been very little change in the treatment regime for young patients with rhabdomyosarcoma. We’re looking for more effective, targeted therapy with fewer long term side effects.